title: Successful correction of hemophilia by CRISPR/Cas9 genome editing in vivo: delivery vector and immune responses are the key to success.
authors.affiliation: INSERM, UMR 1064-Center for Research in Transplantation and Immunology, Nantes, France ITUN, CHU Nantes, Nantes, France Faculté de Médecine, Université de Nantes, Nantes, France.
authors.forename: Tuan Huy
authors.initials: TH
authors.lastname: Nguyen
authors.affiliation: INSERM, UMR 1064-Center for Research in Transplantation and Immunology, Nantes, France ITUN, CHU Nantes, Nantes, France Faculté de Médecine, Université de Nantes, Nantes, France.
authors.forename: Ignacio
authors.identifier: 0000-0001-8700-5645
authors.initials: I
authors.lastname: Anegon
mesh_terms: D064113:CRISPR-Cas Systems; D064112:Clustered Regularly Interspaced Short Palindromic Repeats; D000072669:Gene Editing; D016678:Genome; D006467:Hemophilia A / Q000235:genetics; D006801:Humans