title: The Randomized Blind Start Trial: Evaluation of A New Study Design for Assessing Clinical Outcomes in Rare and Heterogeneous Patient Populations.
authors.affiliation: Analysis Group, Inc., Boston, MA, USA.
authors.forename: J
authors.initials: J
authors.lastname: Signorovitch
authors.affiliation: Analysis Group Inc., Boston, MA, USA.
authors.forename: R
authors.initials: R
authors.lastname: Ayyagari
authors.affiliation: Ultragenyx Pharmaceutical Inc., Novato, CA, USA.
authors.forename: E
authors.initials: E
authors.lastname: Kakkis