title: MEDICINE. Paying for future success in gene therapy.
authors.affiliation: Dana Farber Cancer Institute and Boston Children's Hospital, Howard Hughes Medical Institute, Harvard Medical School, Boston, MA 02115, USA. stuart_orkin@dfci.harvard.edu philip@thirdrockventures.com.
authors.forename: Stuart H
authors.initials: SH
authors.lastname: Orkin
authors.affiliation: Third Rock Ventures, Boston, MA 02116, USA. stuart_orkin@dfci.harvard.edu philip@thirdrockventures.com.
authors.forename: Philip
authors.initials: P
authors.lastname: Reilly
mesh_terms: D000755:Anemia, Sickle Cell / Q000628:therapy; D003550:Cystic Fibrosis / Q000628:therapy; D005544:Forecasting; D005776:Gaucher Disease / Q000628:therapy; D015316:Genetic Therapy / Q000191:economics* / Q000639:trends*; D017048:Health Care Costs; D006467:Hemophilia A / Q000628:therapy; D006801:Humans; D016896:Treatment Outcome