title: Seeking a Cure for One of the Rarest Diseases: Progeria.
authors.affiliation: From Medical Genomics and Metabolic Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD. francis.collins3@nih.gov.
authors.forename: Francis S
authors.initials: FS
authors.lastname: Collins
mesh_terms: D006801:Humans; D034904:Lamin Type A / Q000235:genetics*; D009154:Mutation; D011371:Progeria
chemical_list: D034904:Lamin Type A
keywords: Editorials; everolimus; lamin type A; lonafarnib; morpholinos; progeria; rare diseases; translational medical research