title: Lysosomal storage disorders: 4 big questions.
authors.forename: Michael
authors.initials: M
authors.lastname: Eisenstein
mesh_terms: D001812:Blood-Brain Barrier / Q000378:metabolism; D002986:Clinical Trials as Topic / Q000379:methods; D055808:Drug Discovery; D056947:Enzyme Replacement Therapy; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000201:enzymology / Q000473:pathology* / Q000503:physiopathology / Q000628:therapy*; D008247:Lysosomes / Q000378:metabolism*; D019636:Neurodegenerative Diseases / Q000201:enzymology / Q000235:genetics / Q000503:physiopathology / Q000628:therapy; D051844:alpha-Synuclein / Q000378:metabolism
chemical_list: D051844:alpha-Synuclein