Eteplirsen (Exondys 51) for duchenne muscular dystrophy.
D061605:Administration, Intravenous; D002986:Clinical Trials as Topic / Q000379:methods; D006801:Humans; D060172:Morpholinos / Q000008:administration & dosage*; D020388:Muscular Dystrophy, Duchenne / Q000175:diagnosis / Q000188:drug therapy* / Q000235:genetics
D060172:Morpholinos; C000611335:eteplirsen