title: Survival and Developmental Milestones Among Pompe Registry Patients with Classic Infantile-Onset Pompe Disease with Different Timing of Initiation of Treatment with Enzyme Replacement Therapy.
authors.affiliation: National Taiwan University Hospital, Taipei, Taiwan.
authors.forename: Yin-Hsiu
authors.initials: YH
authors.lastname: Chien
authors.affiliation: Department of Pediatrics & Center for Lysosomal and Metabolic Diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Ans
authors.initials: A
authors.lastname: van der Ploeg
authors.affiliation: Manchester Center for Genomic Medicine, CMFT, University of Manchester, UK.
authors.forename: Simon
authors.initials: S
authors.lastname: Jones
authors.affiliation: Department of Pediatrics, University of Florida, Gainesville, FL, USA.
authors.forename: Barry
authors.initials: B
authors.lastname: Byrne
authors.affiliation: Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.
authors.forename: Ashok
authors.initials: A
authors.lastname: Vellodi
authors.affiliation: Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
authors.forename: Nancy
authors.initials: N
authors.lastname: Leslie
authors.affiliation: University of Mainz, Mainz, Germany.
authors.forename: Eugen
authors.initials: E
authors.lastname: Mengel
authors.affiliation: Emory University School of Medicine, Atlanta, GA, USA.
authors.forename: Suma P
authors.initials: SP
authors.lastname: Shankar
authors.affiliation: Children's National Medical Center, Washington, DC, USA.
authors.forename: Pranoot
authors.initials: P
authors.lastname: Tanpaiboon
authors.affiliation: Wayne State University School of Medicine, Detroit, MI, USA.
authors.forename: David W
authors.initials: DW
authors.lastname: Stockton
authors.affiliation: Charite Universitaetsmedizin Berlin, Berlin, Germany.
authors.forename: Julia B
authors.initials: JB
authors.lastname: Hennermann
authors.affiliation: Genzyme, a Sanofi company, Cambridge, MA, USA.
authors.forename: Zsuzsanna
authors.initials: Z
authors.lastname: Devecseri
authors.affiliation: Genzyme, a Sanofi company, Cambridge, MA, USA.
authors.forename: Judy
authors.initials: J
authors.lastname: Kempf
authors.affiliation: Genzyme, a Sanofi company, Cambridge, MA, USA.
authors.forename: Joan
authors.initials: J
authors.lastname: Keutzer
authors.affiliation: Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC, USA.
authors.forename: Priya
authors.initials: P
authors.lastname: Kishnani