title: Personalized models reveal mechanistic and therapeutic insights into CEP290-associated Leber congenital amaurosis.
authors.affiliation: Center for Advanced Retinal and Ocular Therapeutics, F.M. Kirby Center for Molecular Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA 19104, USA.
authors.forename: Devin S
authors.initials: DS
authors.lastname: McDougald
authors.affiliation: Gene Editing Institute, Center for Translational Cancer Research, Helen F. Graham Cancer Center & Research Institute, Christiana Care Health System, Newark, DE 19702, USA.
authors.forename: Eric
authors.initials: E
authors.lastname: Kmiec
authors.affiliation: Center for Advanced Retinal and Ocular Therapeutics, F.M. Kirby Center for Molecular Ophthalmology, Scheie Eye Institute, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA 19104, USA.
authors.forename: Jason A
authors.initials: JA
authors.lastname: Mills