title: Lentiviral Stem Cell Gene Therapy for Pompe Disease.
authors.affiliation: Department of Hematology, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Qiushi
authors.initials: Q
authors.lastname: Liang
authors.affiliation: Center for Lysosomal and Metabolic Diseases & Department of Clinical Genetics, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Merel
authors.initials: M
authors.lastname: Stok
authors.affiliation: Department of Hematology, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Yvette
authors.initials: Y
authors.lastname: van Helsdingen
authors.affiliation: Department of Hematology, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Guus
authors.initials: G
authors.lastname: van der Velden
authors.affiliation: Department of Genetics, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Ed
authors.initials: E
authors.lastname: Jacobs
authors.affiliation: Department of Experimental Cardiology, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Dirk
authors.initials: D
authors.lastname: Duncker
authors.affiliation: Center for Lysosomal and Metabolic Diseases & Department of Clinical Genetics, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Arnold
authors.initials: A
authors.lastname: Reuser
authors.affiliation: Center for Lysosomal and Metabolic Diseases & Department of Clinical Genetics, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Ans
authors.initials: A
authors.lastname: van der Ploeg
authors.affiliation: Hospital Pharmacy, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Arnold
authors.initials: A
authors.lastname: Vulto
authors.affiliation: Department of Hematology, Erasmus MC University Medical Center, Rotterdam, Netherlands.
authors.forename: Niek P
authors.initials: NP
authors.lastname: van Til
authors.affiliation: Hacettepe University, Stem Cell Research and Development Center, Ankara, Turkey.
authors.forename: Gerard
authors.initials: G
authors.lastname: Wagemaker