title: Eteplirsen therapy for Duchenne muscular dystrophy: skipping to the front of the line.
authors.affiliation: Division of Neurology and Program for Genetics and Genome Biology, Hospital for Sick Children, 555 University Avenue, Toronto, Ontario, Canada, M5G 1X8.
authors.forename: James J
authors.initials: JJ
authors.lastname: Dowling
mesh_terms: D000293:Adolescent; D002648:Child; D002986:Clinical Trials as Topic; D017353:Gene Deletion; D006801:Humans; D008297:Male; D060172:Morpholinos / Q000008:administration & dosage / Q000494:pharmacology*; D020388:Muscular Dystrophy, Duchenne / Q000188:drug therapy*; D016376:Oligonucleotides, Antisense
chemical_list: D060172:Morpholinos; D016376:Oligonucleotides, Antisense; C000611335:eteplirsen