authors.affiliation: Institut Cochin, Faculté de Médecine Paris Descartes, Paris, France.
authors.forename: Jean-Claude
authors.initials: JC
authors.lastname: Kaplan
mesh_terms: D017277:Drug Approval / Q000331:legislation & jurisprudence*; D005091:Exons; D006801:Humans; D060172:Morpholinos / Q000627:therapeutic use*; D020388:Muscular Dystrophy, Duchenne / Q000188:drug therapy* / Q000235:genetics; D010297:Paris; D014481:United States; D014486:United States Food and Drug Administration
chemical_list: D060172:Morpholinos; C000611335:eteplirsen