title: Battle over rare disease drug ensnares NIH.
authors.forename: Meredith
authors.initials: M
authors.lastname: Wadman
mesh_terms: D003505:Cyclodextrins / Q000008:administration & dosage / Q000627:therapeutic use*; D017277:Drug Approval; D016503:Drug Delivery Systems; D006801:Humans; D000072666:National Center for Advancing Translational Sciences (U.S.); D052556:Niemann-Pick Disease, Type C / Q000188:drug therapy*; D016032:Randomized Controlled Trials as Topic; D035583:Rare Diseases / Q000188:drug therapy*; D014481:United States
chemical_list: D003505:Cyclodextrins