title: Eteplirsen Approved for Duchenne Muscular Dystrophy: The FDA Faces a Difficult Choice.
authors.affiliation: Member, Editorial Board.
authors.forename: Cy A
authors.initials: CA
authors.lastname: Stein
mesh_terms: D017277:Drug Approval; D006801:Humans; D008297:Male; D060172:Morpholinos / Q000627:therapeutic use*; D020388:Muscular Dystrophy, Duchenne / Q000188:drug therapy*; D009841:Oligonucleotides; D014481:United States; D014486:United States Food and Drug Administration
chemical_list: D060172:Morpholinos; D009841:Oligonucleotides; C000611335:eteplirsen