title: Nusinersen, an antisense oligonucleotide drug for spinal muscular atrophy.
authors.affiliation: Departments of Pharmacology and Biochemistry, UT Southwestern, Dallas, Texas, USA.
authors.forename: David R
authors.initials: DR
authors.lastname: Corey
mesh_terms: D000818:Animals; D055808:Drug Discovery / Q000379:methods / Q000639:trends*; D006801:Humans; D009134:Muscular Atrophy, Spinal / Q000175:diagnosis / Q000188:drug therapy* / Q000503:physiopathology; D009841:Oligonucleotides / Q000627:therapeutic use*; D016376:Oligonucleotides, Antisense / Q000627:therapeutic use*
chemical_list: D009841:Oligonucleotides; D016376:Oligonucleotides, Antisense; C000590926:nusinersen