title: Genome Editing for Sickle Cell Disease: A Little BCL11A Goes a Long Way.
authors.affiliation: Department of Biochemistry and Molecular Biology, College of Medicine, University of Florida, Gainesville, FL 32610, USA; UF Health Cancer Center, Center for Epigenetics, Genetics Institute, University of Florida, Gainesville, FL 32610, USA.
authors.forename: Mir A
authors.initials: MA
authors.lastname: Hossain
authors.affiliation: Department of Biochemistry and Molecular Biology, College of Medicine, University of Florida, Gainesville, FL 32610, USA; UF Health Cancer Center, Center for Epigenetics, Genetics Institute, University of Florida, Gainesville, FL 32610, USA. Electronic address: jbungert@ufl.edu.
authors.forename: Jörg
authors.initials: J
authors.lastname: Bungert
mesh_terms: D000755:Anemia, Sickle Cell / Q000235:genetics / Q000628:therapy*; D064113:CRISPR-Cas Systems; D002352:Carrier Proteins / Q000235:genetics*; D000072669:Gene Editing / Q000379:methods*; D015316:Genetic Therapy / Q000379:methods; D006801:Humans; D009154:Mutation; D009687:Nuclear Proteins / Q000235:genetics*; D012097:Repressor Proteins; D000075804:Zinc Finger Nucleases / Q000378:metabolism
chemical_list: C486563:BCL11A protein, human; D002352:Carrier Proteins; D009687:Nuclear Proteins; D012097:Repressor Proteins; D000075804:Zinc Finger Nucleases