title: Rounding up sickle cells with gene therapy.
abstract: A report of a patient treated with ex vivo lentiviral gene transfer to hematopoietic stem cells shows the promise of gene therapy for sickle cell anemia.
authors.affiliation: Department of Ophthalmology, University of Pittsburgh, Pittsburgh, PA 15213, USA. Email: lbyrne@pitt.edu.
authors.forename: Leah
authors.initials: L
authors.lastname: Byrne
mesh_terms: D000755:Anemia, Sickle Cell; D015316:Genetic Therapy; D005822:Genetic Vectors; D006412:Hematopoietic Stem Cells; D006801:Humans