Systemic AAV Gene Therapy Close to Clinical Trials for Several Neuromuscular Diseases.
Neuromuscular Diseases Group, Department of Comparative Biomedical Sciences, Royal Veterinary College, Royal College Street, London NW1 0TU, UK. Electronic address: dwells@rvc.ac.uk.
Dominic J
DJ
Wells
D000229:Dependovirus / Q000235:genetics*; D015316:Genetic Therapy; D005822:Genetic Vectors; D006801:Humans; D009468:Neuromuscular Diseases