title: Effects of Lumacaftor/Ivacaftor in a Pediatric Cohort Homozygous for F508del-CFTR.
authors.affiliation: 1 Department of Pediatrics and.|2 Department of Cellular and Molecular Physiology Yale School of Medicine New Haven, Connecticut.
authors.forename: Marie E
authors.identifier: 0000-0002-0567-6048
authors.initials: ME
authors.lastname: Egan
mesh_terms: D000627:Aminophenols; D000631:Aminopyridines; D052117:Benzodioxoles; D002648:Child; D003550:Cystic Fibrosis; D019005:Cystic Fibrosis Transmembrane Conductance Regulator; D006801:Humans; D015363:Quinolones
chemical_list: D000627:Aminophenols; D000631:Aminopyridines; D052117:Benzodioxoles; D015363:Quinolones; D019005:Cystic Fibrosis Transmembrane Conductance Regulator; C545203:ivacaftor; C569105:lumacaftor