Infantile Pompe-rhGAA treated - C
source_name
3D engineered tissue, myobundle
tissue
engineered skeletal muscle
culture age
2 weeks of 3D differentiation culture
genotype
c.1210G>A, c.2481+102_2646+31del
treatment
Treated with 2ug/ml rhGAA (from Sanofi Genzyme) every other day during second week of 3D differentiation