BCL11A ZFN editing in human CD3+ cells purified from murine bone marrow at week 19 post-engraftment
Homo sapiens
BCL11A ZFN-edited dual-agent mobilized HSC from an healthy donor were engrafted into immune-deficient NOD scid gamma (NSG) mice. Human CD3+CD45+ cells were purified from bone marrow collected at week 19.